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HomeFocus → CRISPR fixes disease gene in viable human embryos

CRISPR fixes disease gene in viable human embryos Print E-mail
Written by Heidi Ledford | Nature   
Friday, 04 August 2017 14:54

An international team of researchers has used CRISPR-Cas9 gene editing - a technique that allows scientists to make precise changes to genomes with relative ease - to correct a disease-causing mutation in dozens of viable human embryos. The study represents a significant improvement in efficiency and accuracy over previous efforts.

The researchers targeted a mutation in a gene called MYBPC3. Such mutations cause the heart muscle to thicken - a condition known as hypertrophic cardiomyopathy that is the leading cause of sudden death in young athletes. The mutation is dominant, meaning that a child need inherit only one copy of the mutated gene to experience its effects.

Last Updated on Monday, 28 August 2017 16:15
 


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